Tag: #aav

Engineered miniature CRISPR achieves >80% editing in human cells and could fit inside AAV

Engineered miniature CRISPR raised editing in human cells from <10% to >80% and stays small enough to fit in AAV vectors — tests remain in cells.

#gene-editing, #crispr, #aav, #biotechnology

Iranian researchers use AI to design kidney-targeted viral shells for gene therapy

A preprint describes AAVGen, an AI system that generates adeno-associated virus capsids predicted to better target kidneys—so far only in silico.

#genetherapy, #ai, #kidney, #aav