Tag: #crispr

After One Baby’s Custom CRISPR Rescue, a Startup Bets on Made-to-Order Gene Editing

A one-off CRISPR therapy saved a baby with a lethal mutation. Now a Doudna-backed startup and a new FDA pathway aim to scale bespoke gene medicines.

#crispr, #geneediting, #rarediseases, #fda, #biotech

CRISPR-Edited ‘Off-the-Shelf’ CAR-T Cells Show Early Promise Against Recurrent Glioblastoma in Small China Trial

In a five-patient phase 1 study, intrathecal CRISPR-edited donor CAR-T cells appeared safe and shrank recurrent high-grade gliomas.

#glioblastoma, #cart, #crispr, #immunotherapy, #clinicaltrials

Breakthrough CRISPR Gene Therapy Casgevy Gains Global Approval for Blood Disorders

CRISPR therapy Casgevy approved in UK, US, EU to treat sickle cell and beta-thalassemia, marking a gene-editing milestone.

#genetherapy, #crispr, #sicklecell, #betathalassemia

AI Revolutionizes Gene Editing with Novel Tools

AI-designed gene editing tools enhance precision in genetic modifications, raising ethical and regulatory considerations.

#ai, #geneediting, #biotechnology, #crispr, #healthcare

First Successful Personalized CRISPR Gene Therapy Offers New Hope for Rare Genetic Diseases

Nine-month-old receives groundbreaking CRISPR therapy for rare genetic disorder, marking a milestone in precision medicine.

#CRISPR, #genetherapy, #rarediseases, #precisionmedicine

Biotech Firm Announces Birth of Genetically Engineered Wolf Pups with Dire Wolf Traits

Colossal Biosciences has birthed wolf pups with dire wolf traits, sparking ethical debates on de-extinction efforts.

#biotechnology, #de-extinction, #genetic engineering, #dire wolves, #crispr

FDA Approves First CRISPR-Based Gene-Editing Therapy for Sickle Cell Disease

FDA approves Casgevy, the first CRISPR-based therapy, offering hopes for sickle cell disease patients. A milestone in gene-editing breakthroughs.

#health, #CRISPR, #gene-editing, #sickle cell disease, #FDA approval